Tag Archives: healthcare

Webinar Today: Comparative Effectiveness Research


As we continue to see new strides in biopharmaceutical innovation, there is increasing value in having more information on how specific treatments affect patients.  This is the intention behind comparative effectiveness research, which can play a critical role in health care decision-making. Later today, experts will be examining the relationship between comparative effectiveness research and the way health care decisions may be made in the future.  The National Pharmaceutical Council (NPC) will be hosting a Read More >

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New PhRMA Report: A Decade of Innovation in Rare Diseases


Today, the Pharmaceutical Research and Manufacturers of America (PhRMA) released “A Decade of Innovation in Rare Diseases,” which highlights 10 years of progress in understanding rare diseases and drug development resulting in groundbreaking therapies. According to the report, more than 230 new medicines to treat rare or “orphan” diseases were approved by the U.S. Food and Drug Administration (FDA) in the last decade, and there are currently more than 450 orphan drugs in development. The Read More >

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Biotech Could Miss a Multi-Billion Dollar Opportunity in Rare Disease


Drug development is expensive.  Drug development is risky.  Drug development takes a long time. The key to changing this is leveraging the fact that no one is more motivated to eliminate rare disease than those who are directly affected by it. I know this because, as the founder of Give RARE, I have talked to parents of children with Tay Sachs disease who know their children will die within a few years unless something changes.  Read More >

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World Rare Disease Day Celebrates Patient Advocacy and Activism Around The Globe


Global Genes™ and the identifiable Blue Denim Genes Ribbon™ provides opportunity to show support and help build awareness Global Genes, a leading patient advocacy organization with the mission to eliminate the challenges of rare disease, is inviting industry partners to support the eighth annual World Rare Disease Day. World Rare Disease Day is a day of advocacy to call attention to rare disease in the United States and around the globe. Created by European organization Read More >

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Patients Remain the Focus for the Future of Personalizing Oncology


The 17th Annual BIO CEO & Investor Conference, being held at the Waldorf Astoria in New York City, kicked off this morning with an interactive panel of industry heavyweights discussing the growing trend to personalize oncology treatments with molecular diagnostics. Moderated by Michael King, Managing Director, Senior Research Analyst, JMP Securities. Michael helped steer the group of experts as they discussed enabling broader matching of patient-cancer-therapy, lessons learned from the Cancer Genome Atlas and the potential Read More >

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