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BIO Illustrates the Success of the Orphan Drug Act

The numbers might surprise you. Approximately 7,000 rare diseases are known to exist, and approximately …

President’s Joint Address to Congress Could Be Huge for Biotech Industry

“We stand at the birth of a new millennium, ready to unlock the mysteries of …

My Friend Liz’s Condition Is Rare; So Is Her Passion and Her Spirit

I have known Liz Kennerley for more than 20 years, since before the onset of …

NORD President: Congress must act now to help 15 million sick children

Writing in The Hill, National Organization for Rare Disorders (NORD) President and CEO Peter Saltonstall …

Climbing the Same Mountain: How Rare Disease Day Has Changed Our World

Rare Disease Day has a short history in the arena of national awareness events. It’s …

Getting Ready for #RDD2015 (Rare Disease Day 2015)

Rare Disease Day is just around the corner on February 28th. R&D investment into rare …

Biotech Could Miss a Multi-Billion Dollar Opportunity in Rare Disease

Drug development is expensive.  Drug development is risky.  Drug development takes a long time. The …

Mito What???

Mitochondrial Disease: The Most Common Disease You’ve Probably Never Heard of… About 20 years ago, …