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The Washington Post Unfairly Attacks The Orphan Drug Act

The Orphan Drug Act has been a tremendous success and addressed a market failure by …

Complexities of Rare Diseases Take the Spotlight at BIO

Global Genes Founder & CEO Nicole Boice opened the BIO 2015 Orphan & Rare Disease …

New PhRMA Report: A Decade of Innovation in Rare Diseases

Today, the Pharmaceutical Research and Manufacturers of America (PhRMA) released “A Decade of Innovation in …

Mito What???

Mitochondrial Disease: The Most Common Disease You’ve Probably Never Heard of… About 20 years ago, …

Rare Disease Day 2014: Joining Together for Better Care

There are more than 6,000 different rare diseases affecting over 60 million people across Europe …

The Ethics of the Market Access Debate

At the core of the market access conversation lies the question of value. How much …

A Bright Future for Orphan Disease Indications

In celebration of National Rare Disease Day BIO’s Industry Analysis team took a look at recently-approved …

Navigating the Rare Disease World

The international orphan drug marketplace is expected to grow some 30 percent by 2014, fueled …

Rare Disease Day: Families and Advocacy Groups Drive Treatments for Rare Diseases

Today, we celebrate Rare Disease Day to recognize the path to treatments and cures is …

Orphan Drugs: Making Rare Diseases Rarer

A panel at the BIO CEO & Investor Conference provided an analysis of the thriving …