Tag: rare diseases
The Washington Post Unfairly Attacks The Orphan Drug Act
The Orphan Drug Act has been a tremendous success and addressed a market failure by …
Complexities of Rare Diseases Take the Spotlight at BIO
Global Genes Founder & CEO Nicole Boice opened the BIO 2015 Orphan & Rare Disease …
New PhRMA Report: A Decade of Innovation in Rare Diseases
Today, the Pharmaceutical Research and Manufacturers of America (PhRMA) released “A Decade of Innovation in …
Mito What???
Mitochondrial Disease: The Most Common Disease You’ve Probably Never Heard of… About 20 years ago, …
Rare Disease Day 2014: Joining Together for Better Care
There are more than 6,000 different rare diseases affecting over 60 million people across Europe …
The Ethics of the Market Access Debate
At the core of the market access conversation lies the question of value. How much …
A Bright Future for Orphan Disease Indications
In celebration of National Rare Disease Day BIO’s Industry Analysis team took a look at recently-approved …
Navigating the Rare Disease World
The international orphan drug marketplace is expected to grow some 30 percent by 2014, fueled …
Rare Disease Day: Families and Advocacy Groups Drive Treatments for Rare Diseases
Orphan Drugs: Making Rare Diseases Rarer
A panel at the BIO CEO & Investor Conference provided an analysis of the thriving …