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Onyx CEO One of 25 Most Influential People in Biopharm Today According to FierceBiotech

After a stellar year, as evidenced by inclusion in the second annual FierceBiotech “25 Most …

FDASIA: A Step Forward for Patients

Earlier this year, Congress passed and President Obama signed the FDA Safety and Innovation Act …

BIO Investor Forum - Raring to Go: The Race to Treat Ultra-Rare Diseases

The signing of FDASIA by President Obama in July reinforces the country’s commitment to fostering …

New Rare Disease Miniseries

Calling all biopharma researchers! Morning show “The Balancing Act” is producing a miniseries called “Roulette …

FDA Safety and Innovation Act: A Step Forward for Patients With Rare Diseases

By Peter L. Saltonstall, President and CEO, National Organization for Rare Disorders (NORD) The Food …

People With Rare Diseases Face a Host of Unique Challenges

By Dennis Jackman, Senior Vice President, Public Affairs, CSL Behring People with rare and serious …

2012 Orphan Disease Forum: Addressing Today’s Opportunities and Challenges

If all of the people with rare disease lived in one country, it would be …

International Rare Disease Day: Join the Movement

By Nicole Boice, President and Founder, RARE Project Being diagnosed with any illness can be …

Stopping ALS: An interview with Dr. Perrin from ALS TDI

What is ALS? How widespread is the disease? Are there any treatments for ALS? Amyotrophic …

When RARE is not so RARE!

By Nicole Boice, Founder/President, RARE Project Did you know that there is a community of …